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grnball Overview of neurodegeneration with brain iron accumulation nbia disorders

grnball Case Report
Late Onset Atypical Pantothenate-Kinase-Associated Neurodegeneration

CLINICAL TRIALS
Currently there are four clinical studies underway:

grnball Brain Perfusion in Pantothenate Kinase-associated Neurodegeneration (PKAN)

grnball A Two-arm Efficacy and Safety Study of Deferiprone in Patients With Pantothenate Kinase-associated Neurodegeneration (PKAN)

grnball Long-term Deferiprone Treatment in Patients With Pantothenate Kinase-Associated Neurodegeneration (TIRCON-EXT)

grnball Ferrochelating Treatment in Patients Affected by Neurodegeneration With Brain Iron Accumulation (NBIA)

OTHER RESOURCES

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nbia rareconnect tircon
nbiaworld nord rareRare Disease Day